Gene therapy

Ils ont réécrit son ADN pour soigner une maladie rare

They rewrote his DNA to treat a rare disease

EP 251: Cracking the delivery barrier in genetic medicine with Jagesh Shah of Mirai Bio

Fallece Niña de 6 Años Tras Terapia Genética en China - CIENCIA SIMPLIFICADA EP#85

6-Year-Old Girl Dies After Gene Therapy in China - CIENCIA SIMPLIFICADA EP#85

EP 244: Building the first n-of-1 ASO: The new frontier of rare disease with Timothy Yu of Boston...

EP 244: Building the first n-of-1 ASO with Timothy Yu of Boston Children’s Hospital

Gene Therapy for Anxiety? Precision Psychiatry through CRISPR & RNA

EP 241: The hard-won lessons behind Encoded Therapeutics’ Dravet syndrome gene therapy [Re-run]

LA THÉRAPIE GÉNIQUE

GENE THERAPY

From Natural History to Gene Therapy: The Future of Danon Disease Research

L’hôpital du futur (21) - 2025-2026

The hospital of the future (21) - 2025-2026

EP 226: Scaling AAV gene therapy with David Dismuke of Forge Biologics & Steven Gray of UTSW

EP 225: Lessons from 20 years of building ocular gene therapies with Daniel Chung of Beacon Tx

Urgent Advocacy for 2026 FDA Approval of Hunter Syndrome Gene Therapy & Treatments

【Personalized Nucleic Acid Therapy】

The science of delivering cures straight to your cells | Eric Kelsic

EP 213: Inside the science of hearing loss and gene therapy for deafness with Ellen Reisinger of ...

EP 208: Gene therapy at a crossroads: Successes, concerns, and the path forward

EP 201: The gene therapy playbook: Successes, setbacks, and the path forward with Richard Wilson ...

Le VACCIN COVID n'était que le début : Comment ces Nanoparticules vont vaincre le CANCER

The COVID VACCINE was just the beginning: How these Nanoparticles will defeat CANCER

EP 213: Inside the science of hearing loss and gene therapy for deafness with Ellen Reisinger

EP 208: Gene therapy at a crossroads: Successes, concerns, and the path forward

Unlocking the Future of Gene Therapy

Nathalie Mignet - Nanomédicaments et nanoparticules lipidiques pour la délivrance d'acide nucléique

Nathalie Mignet - Nanomedicines and lipid nanoparticles for nucleic acid delivery

EP 201: The gene therapy playbook: Success, setbacks, the path forward | Richard Wilson of Astellas

Understanding RNA Neurotherapeutics

Genetic Therapeutics, DNA & RNA tx

Targeted Therapeutics, Oligonucleotide Conjugates for Transfection, Nucleic Acid Therapeutics

Genetic Medicine, Understanding Antisense Oligonucleotides (ASOs), Design, modifications & in viv...

Genetics: L29-C, ASO treatment for SMA1 (Recommend 1.5x Speed)

Gene Therapy: AAV Biology (Recommend 1.5x Speed)

Gene therapy and SMA1 (Recommend 1.5x Speed)

Competitive intelligence study of a non-viral vector for gene therapy of Parkinson´s disease

Game Changing Therapeutic Technology

Whatever Happened to Gene Therapy

Stem Cells in Gene Therapy

Genetic Surgery: Curing Hemophilia

Stem Cells in Gene Therapy